Generation of clinical grade recombinant adeno-associated virus

Recombinant adeno-associated viruses (rAAV) remain one of the most encouraging gene therapy vectors for treating patients with genetic abnormalities. rAAV can safely deliver long-lasting expression of a therapeutic transgene to a wide range of cell types. One challenge with therapeutic rAAV is the...

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Bibliographic Details
Main Author: Tie, Mark
Other Authors: Offner, Gwynneth
Language:en_US
Published: 2018
Subjects:
Online Access:https://hdl.handle.net/2144/31279