Responsiveness of outcome measures in myotonic dystrophy type 1

Abstract Objective As myotonic dystrophy type 1(DM1) evolves slowly and interventional trials often have a short duration, responsive outcomes in DM1 are needed. The objective of this study was to determine the responsiveness of muscle strength, balance, and functional mobility measurements after a...

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Bibliographic Details
Main Authors: Kirsten L. Knak, Aisha M. Sheikh, Nanna Witting, John Vissing
Format: Article
Language:English
Published: Wiley 2020-08-01
Series:Annals of Clinical and Translational Neurology
Online Access:https://doi.org/10.1002/acn3.51129