Sequential everolimus for angiomyolipoma associated with tuberous sclerosis complex: a prospective cohort study

Abstract Background To evaluate the efficacy, safety and health economics of sequential everolimus in treating angiomyolipoma (AML) associated with tuberous sclerosis complex (TSC). Methods In this prospective cohort study, patients met the inclusion criteria received standard or sequential treatmen...

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Bibliographic Details
Main Authors: Liangyou Gu, Cheng Peng, Fan Zhang, Cunjin Fang, Gang Guo
Format: Article
Language:English
Published: BMC 2021-06-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Online Access:https://doi.org/10.1186/s13023-021-01913-2