An overview of the impact of rare disease characteristics on research methodology

An overview of the impact of rare disease characteristics on research methodology

Abstract Background About 30 million individuals in the United States are living with a rare disease, which by definition have a prevalence of 200,000 or fewer cases in the United States ([National Organization for Rare Disorders], [About NORD], [2016]). Disease heterogeneity and geographic dispersi...

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Bibliographic Details
Main Authors: Danielle Whicher, Sarah Philbin, Naomi Aronson
Format: Article
Language:English
Published: BMC 2018-01-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Rare disease
Research design
Orphan disease
Experimental designs
Registries
Online Access:http://link.springer.com/article/10.1186/s13023-017-0755-5

Internet

http://link.springer.com/article/10.1186/s13023-017-0755-5

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