A tutorial on the use of exploratory efficacy outcomes in uncontrolled phase I cell therapy trials
Abstract Phase I cell therapy clinical trials evaluate the safety of novel biologic treatments and are often uncontrolled. Many of these studies also include exploratory efficacy outcome measures, which are frequently continuous measures of disease state or severity, or participant‐reported measures...
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| Format: | Article |
| Language: | English |
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Wiley
2020-11-01
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| Series: | Stem Cells Translational Medicine |
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| Online Access: | https://doi.org/10.1002/sctm.20-0116 |