CRISPR to the Rescue: Advances in Gene Editing for the <i>FMR1</i> Gene

Gene-editing using Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) is promising as a potential therapeutic strategy for many genetic disorders. CRISPR-based therapies are already being assessed in clinical trials, and evaluation of this technology in Fragile X syndrome has been pe...

Full description

Bibliographic Details
Main Authors: Carolyn M. Yrigollen, Beverly L. Davidson
Format: Article
Language:English
Published: MDPI AG 2019-01-01
Series:Brain Sciences
Subjects:
Online Access:https://www.mdpi.com/2076-3425/9/1/17