CASE SERIES OF PATIENTS UNDER BIWEEKLY TREATMENT WITH LARONIDASE: A REPORT OF A SINGLE CENTER EXPERIENCE

CASE SERIES OF PATIENTS UNDER BIWEEKLY TREATMENT WITH LARONIDASE: A REPORT OF A SINGLE CENTER EXPERIENCE

ABSTRACT Objective: To report the stabilization of urinary glycosaminoglicans (GAG) excretion and clinical improvements in patients with mucopolysaccharidosis type I (MPS I) under an alternative dose regimen of laronidase of 1.2 mg/kg every other week. Methods: We participated in a dose-optimiza...

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Bibliographic Details
Main Authors: Sandra Obikawa Kyosen, Leny Toma, Helena Bonciani Nader, Marion Coting Braga, Vanessa Gonçalves Pereira, Sueli Canossa, João Bosco Pesquero, Vânia D’Almeida, Ana Maria Martins
Format: Article
Language:English
Published: Sociedade de Pediatria de São Paulo 2019-05-01
Series:Revista Paulista de Pediatria
Subjects:
Terapia de reposição de enzimas
Erros inatos do metabolismo
Glicosaminoglicanos
Mucopolissacaridose I
Online Access:http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0103-05822019005008106&lng=en&tlng=en

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http://www.scielo.br/scielo.php?script=sci_arttext&pid=S0103-05822019005008106&lng=en&tlng=en

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