Splicing modulation therapy in the treatment of genetic diseases
Virginia Arechavala-Gomeza,1 Bernard Khoo,2 Annemieke Aartsma-Rus3 1Neuromuscular Disorders Group, BioCruces Health Research Institute, Barakaldo, Bizkaia, Spain; 2Endocrinology, Division of Medicine, University College London, London, UK; 3Department of Human Genetics, Leiden University Medical C...
| Main Authors: | , , |
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| Format: | Article |
| Language: | English |
| Published: |
Dove Medical Press
2014-12-01
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| Series: | The Application of Clinical Genetics |
| Online Access: | http://www.dovepress.com/splicing-modulation-therapy-in-the-treatment-of-genetic-diseases-peer-reviewed-article-TACG |