The influence of a polymorphism in the gene encoding angiotensin converting enzyme (ACE) on treatment outcomes in late-onset Pompe patients receiving alglucosidase alfa

by Rena C. Baek, Rachel Palmer, Robert J. Pomponio, Yuefeng Lu, Xiwen Ma, Alison J. McVie-Wylie
Published 2016-09-01

Thematic Review Series: Sphingolipids. Ganglioside GM3 suppresses the proangiogenic effects of vascular endothelial growth factor and ganglioside GD1a*

by Purna Mukherjee, Anthony C. Faber, Laura M. Shelton, Rena C. Baek, Thomas C. Chiles, Thomas N. Seyfried
Published 2008-05-01

AAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival.

by Rena C Baek, Marike L D Broekman, Stanley G Leroy, Laryssa A Tierney, Michael A Sandberg, Alessandra d'Azzo, Thomas N Seyfried, Miguel Sena-Esteves
Published 2010-10-01