Ribitol restores functionally glycosylated α-dystroglycan and improves muscle function in dystrophic FKRP-mutant mice

by Marcela P. Cataldi, Peijuan Lu, Anthony Blaeser, Qi Long Lu
Published 2018-08-01

Polyquaternium-mediated delivery of morpholino oligonucleotides for exon-skipping in vitro and in mdx mice

by Mingxing Wang, Bo Wu, Sapana N Shah, Peijuan Lu, Qilong Lu
Published 2017-01-01

Aminoglycoside Enhances the Delivery of Antisense Morpholino Oligonucleotides In Vitro and in mdx Mice

by Mingxing Wang, Bo Wu, Sapana N. Shah, Peijuan Lu, Qilong Lu
Published 2019-06-01

Saponins as Natural Adjuvant for Antisense Morpholino Oligonucleotides Delivery In Vitro and in mdx Mice

by Mingxing Wang, Bo Wu, Sapana N. Shah, Peijuan Lu, Qilong Lu
Published 2018-06-01

Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP Gene

by Charles Harvey Vannoy, Will Xiao, Peijuan Lu, Xiao Xiao, Qi Long Lu
Published 2017-06-01

ISPD Overexpression Enhances Ribitol-Induced Glycosylation of α-Dystroglycan in Dystrophic FKRP Mutant Mice

by Marcela P. Cataldi, Anthony Blaeser, Peijuan Lu, Victoria Leroy, Qi Long Lu
Published 2020-06-01

Triazine-cored polymeric vectors for antisense oligonucleotide delivery in vitro and in vivo

by Mingxing Wang, Bo Wu, Jason D. Tucker, Sapana N. Shah, Peijuan Lu, Qilong Lu
Published 2020-02-01

Poly(ester amine) Composed of Polyethylenimine and Pluronic Enhance Delivery of Antisense Oligonucleotides In Vitro and in Dystrophic mdx Mice

by Mingxing Wang, Bo Wu, Jason D Tucker, Lauren E Bollinger, Peijuan Lu, Qilong Lu
Published 2016-01-01

Targeted skipping of human dystrophin exons in transgenic mouse model systemically for antisense drug development.

by Bo Wu, Ehsan Benrashid, Peijuan Lu, Caryn Cloer, Allen Zillmer, Mona Shaban, Qi Long Lu
Published 2011-01-01

Evaluation of Amphiphilic Peptide Modified Antisense Morpholino Oligonucleotides In Vitro and in Dystrophic mdx Mice

by Mingxing Wang, Bo Wu, Peijuan Lu, Sapana N. Shah, Jason D. Tucker, Lauren E. Bollinger, Qilong Lu
Published 2017-05-01

Tween 85-Modified Low Molecular Weight PEI Enhances Exon-Skipping of Antisense Morpholino Oligomer In Vitro and in mdx Mice

by Mingxing Wang, Bo Wu, Jason D. Tucker, Sapana N. Shah, Peijuan Lu, Lauren E. Bollinger, Qilong Lu
Published 2017-12-01