Proof of concept for AAV2/5-mediated gene therapy in iPSC-derived retinal pigment epithelium of a choroideremia patient

by Nicolas Cereso, Marie O Pequignot, Lorenne Robert, Fabienne Becker, Valerie De Luca, Nicolas Nabholz, Valerie Rigau, John De Vos, Christian P Hamel, Vasiliki Kalatzis
Published 2014-01-01

A Novel Chromosomal Translocation Identified due to Complex Genetic Instability in iPSC Generated for Choroideremia

by Nejla Erkilic, Vincent Gatinois, Simona Torriano, Pauline Bouret, Carla Sanjurjo-Soriano, Valerie De Luca, Krishna Damodar, Nicolas Cereso, Jacques Puechberty, Rocio Sanchez-Alcudia, Christian P. Hamel, Carmen Ayuso, Isabelle Meunier, Franck Pellestor, Vasiliki Kalatzis
Published 2019-09-01