Viral Vector-Mediated Antisense Therapy for Genetic Diseases

by Marine Imbert, Gabriella Dias-Florencio, Aurélie Goyenvalle
Published 2017-01-01

The Use of Tricyclo-DNA Oligomers for the Treatment of Genetic Disorders

by Philippine Aupy, Lucía Echevarría, Karima Relizani, Aurélie Goyenvalle
Published 2017-12-01

The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery

by Agathe Eckenfelder, Julie Tordo, Arran Babbs, Kay E Davies, Aurélie Goyenvalle, Olivier Danos
Published 2012-01-01

Efficient SMN Rescue following Subcutaneous Tricyclo-DNA Antisense Oligonucleotide Treatment

by Valérie Robin, Graziella Griffith, John-Paul L. Carter, Christian J. Leumann, Luis Garcia, Aurélie Goyenvalle
Published 2017-06-01

Link between MHC Fiber Type and Restoration of Dystrophin Expression and Key Components of the DAPC by Tricyclo-DNA-Mediated Exon Skipping

by Saleh Omairi, Kwan-Leong Hau, Henry Collin-Hooper, Federica Montanaro, Aurelie Goyenvalle, Luis Garcia, Ketan Patel
Published 2017-12-01

Efficacy and Safety Profile of Tricyclo-DNA Antisense Oligonucleotides in Duchenne Muscular Dystrophy Mouse Model

by Karima Relizani, Graziella Griffith, Lucía Echevarría, Faouzi Zarrouki, Patricia Facchinetti, Cyrille Vaillend, Christian Leumann, Luis Garcia, Aurélie Goyenvalle
Published 2017-09-01

Long-Term Efficacy of AAV9-U7snRNA-Mediated Exon 51 Skipping in mdx52 Mice

by Philippine Aupy, Faouzi Zarrouki, Quentin Sandro, Cécile Gastaldi, Pierre-Olivier Buclez, Kamel Mamchaoui, Luis Garcia, Cyrille Vaillend, Aurélie Goyenvalle
Published 2020-06-01

Exon Skipping in a Dysf-Missense Mutant Mouse Model

by Jakub Malcher, Leonie Heidt, Aurélie Goyenvalle, Helena Escobar, Andreas Marg, Cyriaque Beley, Rachid Benchaouir, Michael Bader, Simone Spuler, Luis García, Verena Schöwel
Published 2018-12-01

Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B.

by Simon Krooss, Sonja Werwitzke, Johannes Kopp, Alice Rovai, Dirk Varnholt, Amelie S Wachs, Aurelie Goyenvalle, Annemieke Aarstma-Rus, Michael Ott, Andreas Tiede, Jörg Langemeier, Jens Bohne
Published 2020-04-01

Correction: Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B.

by Simon Krooss, Sonja Werwitzke, Johannes Kopp, Alice Rovai, Dirk Varnholt, Amelie S Wachs, Aurelie Goyenvalle, Annemieke Aartsma-Rus, Michael Ott, Andreas Tiede, Jörg Langemeier, Jens Bohne
Published 2021-01-01

Altered visual processing in the mdx52 mouse model of Duchenne muscular dystrophy

by Mirella Telles Salgueiro Barboni, André Maurício Passos Liber, Anneka Joachimsthaler, Amel Saoudi, Aurélie Goyenvalle, Alvaro Rendon, Jérome E. Roger, Dora Fix Ventura, Jan Kremers, Cyrille Vaillend
Published 2021-05-01

Correction: Impaired Adaptive Response to Mechanical Overloading in Dystrophic Skeletal Muscle

by Pierre Joanne, Christophe Hourdé, Julien Ochala, Yvain Caudéran, Fadia Medja, Alban Vignaud, Etienne Mouisel, Wahiba Hadj-Said, Ludovic Arandel, Luis Garcia, Aurélie Goyenvalle, Rémi Mounier, Daria Zibroba, Kei Sakamato, Gillian Butler-Browne, Onnik Agbulut, Arnaud Ferry
Published 2013-01-01

Correction: Impaired Adaptive Response to Mechanical Overloading in Dystrophic Skeletal Muscle.

by Pierre Joanne, Christophe Hourdé, Julien Ochala, Yvain Caudéran, Fadia Medja, Alban Vignaud, Etienne Mouisel, Wahiba Hadj-Said, Ludovic Arandel, Luis Garcia, Aurélie Goyenvalle, Rémi Mounier, Daria Zibroba, Kei Sakamato, Gillian Butler-Browne, Onnik Agbulut, Arnaud Ferry
Published 2013-01-01

Impaired adaptive response to mechanical overloading in dystrophic skeletal muscle.

by Pierre Joanne, Christophe Hourdé, Julien Ochala, Yvain Caudéran, Fadia Medja, Alban Vignaud, Etienne Mouisel, Wahiba Hadj-Said, Ludovic Arandel, Luis Garcia, Aurélie Goyenvalle, Rémi Mounier, Daria Zibroba, Kei Sakamoto, Gillian Butler-Browne, Onnik Agbulut, Arnaud Ferry
Published 2012-01-01