Allogeneic Haematopoietic Cell Transplantation for Epidermolysis Bullosa: the Dutch Experience

by Katarzyna B. Gostyńska, Vamsi K. Yenamandra, Caroline Lindemans, José Duipmans, Antoni Gostyński, Marcel F. Jonkman, Jaap-Jan Boelens
Published 2018-12-01

Antisense Oligonucleotide-mediated Exon Skipping as a Systemic Therapeutic Approach for Recessive Dystrophic Epidermolysis Bullosa

by Jeroen Bremer, Olivier Bornert, Alexander Nyström, Antoni Gostynski, Marcel F Jonkman, Annemieke Aartsma-Rus, Peter C van den Akker, Anna MG Pasmooij
Published 2016-01-01