A Potential New Therapeutic Approach for Friedreich Ataxia: Induction of Frataxin Expression With TALE Proteins

by Pierre Chapdelaine, Zoé Coulombe, Amina Chikh, Catherine Gérard, Jacques P Tremblay
Published 2013-01-01

An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models

by Catherine Gérard, Xiao Xiao, Mohammed Filali, Zoé Coulombe, Marie Arsenault, Jacques Couet, Juan Li, Marie-Claude Drolet, Pierre Chapdelaine, Amina Chikh, Jacques P Tremblay
Published 2014-01-01