RPGR-associated retinitis pigmentosa : a multi-modal longitudinal study investigating retinal structure and function in preparation for gene therapy trials
RPGR-associated retinitis pigmentosa is among the most severe forms of RP and is an important target for gene therapy trials. There is however a lack of robust clinical data on this condition. The aim of this thesis is therefore to investigate and characterise the natural history with protocol-drive...
Main Author: | Tee, James J. L. |
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Published: |
University College London (University of London)
2018
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Subjects: | |
Online Access: | https://ethos.bl.uk/OrderDetails.do?uin=uk.bl.ethos.763229 |
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