Advancing lentiviral gene therapy vectors for β-thalassaemia
Background: β-thalassaemia is a potentially lethal hereditary anaemia, caused by reduced or absent expression of HBB polypeptide chains of adult haemoglobin (HbA: α2β2). Current curative treatment options are limited to few patients, while alternative, chronic palliative therapy consisting of freque...
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King's College London (University of London)
2015
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| Online Access: | http://ethos.bl.uk/OrderDetails.do?uin=uk.bl.ethos.682197 |