Nanoparticle delivery of CRISPR/Cas9 gene therapy for Wilson's
disease

Nanoparticle delivery of CRISPR/Cas9 gene therapy for Wilson's disease

CRISPR/Cas9 is being investigated by the larger medical and research community to cure genetic disease that place large burden on patients. This new method of Gene Editing has been investigated for addressing unmet medical need in patients with genetic disease. Wilson's...

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Online Access:	http://hdl.handle.net/2047/D20356168

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