Bayesian Approaches for Confirmatory Trials in Rare Diseases: Opportunities and Challenges

The aim of this narrative review is to introduce the reader to Bayesian methods that, in our opinion, appear to be the most important in the context of rare diseases. A disease is defined as rare depending on the prevalence of the affected patients in the considered population, for example, about 1...

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Bibliographic Details
Main Authors: Moreno Ursino, Nigel Stallard
Format: Article
Language:English
Published: MDPI AG 2021-01-01
Series:International Journal of Environmental Research and Public Health
Subjects:
Online Access:https://www.mdpi.com/1660-4601/18/3/1022

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