Diagnosis and management of lysosomal storage disorders. Three key words: early, multidisciplinary, and network
The European Commission on Public Health defines as rare diseases <em>life-threatening or chronically debilitating diseases which are of such low prevalence that special combined efforts are needed to address them</em>...
Main Authors: | Generoso Andria, Giuseppe Limongelli |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2013-02-01
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Series: | Cardiogenetics |
Subjects: | |
Online Access: | http://www.pagepressjournals.org/index.php/cardiogen/article/view/1439 |
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