Disease Progression Modeling to Evaluate the Effects of Enzyme Replacement Therapy on Kidney Function in Adult Patients with the Classic Phenotype of Fabry Disease

Disease Progression Modeling to Evaluate the Effects of Enzyme Replacement Therapy on Kidney Function in Adult Patients with the Classic Phenotype of Fabry Disease

Background/Aims: Fabry disease (FD) is a rare inherited lysosomal storage disease with common and serious kidney complications. Enzyme replacement therapies (ERT) with agalsidase-α and -β were investigated to characterize their therapeutic effect on kidney function in FD patients with Classic phenot...

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Bibliographic Details
Main Authors: Albina Nowak, Gilbert Koch, Uyen Huynh-Do, Martin Siegenthaler, Hans-Peter Marti, Marc Pfister
Format: Article
Language:English
Published: Karger Publishers 2017-02-01
Series:Kidney & Blood Pressure Research
Subjects:
Enzyme replacement therapy
Fabry disease
Classic phenotype
Modeling
Nephropathy
Online Access:http://www.karger.com/Article/FullText/464312

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