Therapy Development by Genome Editing of Hematopoietic Stem Cells

Therapy Development by Genome Editing of Hematopoietic Stem Cells

Accessibility of hematopoietic stem cells (HSCs) for the manipulation and repopulation of the blood and immune systems has placed them at the forefront of cell and gene therapy development. Recent advances in genome-editing tools, in particular for clustered regularly interspaced short palindromic r...

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Bibliographic Details
Main Authors:	Lola Koniali, Carsten W. Lederer, Marina Kleanthous
Format:	Article
Language:	English
Published:	MDPI AG 2021-06-01
Series:	Cells
Subjects:	genome editing hematopoietic stem cell blood disorders gene therapy (GT) monogenic disorder TALEN
Online Access:	https://www.mdpi.com/2073-4409/10/6/1492

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