Advanced therapies for the treatment of hemophilia: future perspectives

<p>Abstract</p> <p>Monogenic diseases are ideal candidates for treatment by the emerging advanced therapies, which are capable of correcting alterations in protein expression that result from genetic mutation. In hemophilia A and B such alterations affect the activity of coagulatio...

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Bibliographic Details
Main Authors: Liras Antonio, Segovia Cristina, Gabán Aline S
Format: Article
Language:English
Published: BMC 2012-12-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Online Access:http://www.ojrd.com/content/7/1/97