Advanced therapies for the treatment of hemophilia: future perspectives
<p>Abstract</p> <p>Monogenic diseases are ideal candidates for treatment by the emerging advanced therapies, which are capable of correcting alterations in protein expression that result from genetic mutation. In hemophilia A and B such alterations affect the activity of coagulatio...
Main Authors: | , , |
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Format: | Article |
Language: | English |
Published: |
BMC
2012-12-01
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Series: | Orphanet Journal of Rare Diseases |
Subjects: | |
Online Access: | http://www.ojrd.com/content/7/1/97 |