Health-economic evaluation of risdiplam (Evrysdi®) in patients with spinal muscular atrophy
Background. Spinal muscular atrophies (SMA) are clinically and genetically heterogenous inherited orphan diseases leading to progressive spinal motoneurons degeneration and loss of function. Risdiplam and nusinersen are both authorized in Russia for pathogenic SMA treatment and included in the list...
Main Authors: | А. S. Kolbin, А. А. Kurylev, Yu. Е. Balykina, М. А. Proskurin, S. А. Mishinova |
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Format: | Article |
Language: | Russian |
Published: |
IRBIS LLC
2021-01-01
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Series: | Фармакоэкономика |
Subjects: | |
Online Access: | https://www.pharmacoeconomics.ru/jour/article/view/511 |
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