Familial amyloidotic polyneuropathy: current and emerging treatment options for transthyretin-mediated amyloidosis

Familial amyloidotic polyneuropathy: current and emerging treatment options for transthyretin-mediated amyloidosis

Ernst HundDepartment of Neurology, University of Heidelberg, Heidelberg, GermanyAbstract: Transthyretin familial amyloid polyneuropathy (TTR-FAP) is a fatal clinical disorder characterized by extracellular deposition of abnormal fibrils derived from misfolded, normally soluble transthyretin (TTR) mo...

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Bibliographic Details
Main Author:	Hund E
Format:	Article
Language:	English
Published:	Dove Medical Press 2012-06-01
Series:	The Application of Clinical Genetics
Online Access:	http://www.dovepress.com/familial-amyloidotic-polyneuropathy-current-and-emerging-treatment-opt-a10151

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