Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease

Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease

Abstract Background It is now acknowledged that the input of patients in health outcome assessment is vital to understanding the impact of diseases and interventions for those diseases. This study is the first report of patient-reported outcome measures (PROM) in a large cohort of patients with type...

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Bibliographic Details
Main Authors: Tama Dinur, Majdolen Istaiti, Dafna Frydman, Michal Becker-Cohen, Jeff Szer, Ari Zimran, Shoshana Revel-Vilk
Format: Article
Language:English
Published: BMC 2020-10-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Gaucher disease
Patients reported outcome
Mobile survey
Adult patients
Quality of life
Online Access:http://link.springer.com/article/10.1186/s13023-020-01544-z

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