Effects of Mini-Dystrophin on Dystrophin-Deficient, Human Skeletal Muscle-Derived Cells

Effects of Mini-Dystrophin on Dystrophin-Deficient, Human Skeletal Muscle-Derived Cells

Background: We are developing a novel therapy for Duchenne muscular dystrophy (DMD), involving the transplantation of autologous, skeletal muscle-derived stem cells that have been genetically corrected to express dystrophin. Dystrophin is normally expressed in activated satellite cells and in differ...

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Bibliographic Details
Main Authors:	Jinhong Meng, John Counsell, Jennifer E. Morgan
Format:	Article
Language:	English
Published:	MDPI AG 2020-09-01
Series:	International Journal of Molecular Sciences
Subjects:	Duchenne muscular dystrophy mini-dystrophin lentivirus promotor
Online Access:	https://www.mdpi.com/1422-0067/21/19/7168

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