Effect of enzyme therapy and prognostic factors in 69 adults with Pompe disease: an open-label single-center study

by de Vries Juna M, van der Beek Nadine AME, Hop Wim CJ, Karstens Francois PJ, Wokke John H, de Visser Marianne, van Engelen Baziel GM, Kuks Jan BM, van der Kooi Anneke J, Notermans Nicolette C, Faber Catharina G, Verschuuren Jan JGM, Kruijshaar Michelle E, Reuser Arnold JJ, van Doorn Pieter A, van der Ploeg Ans T
Published 2012-09-01