Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD

by Barcellini, W., Bianchi, P., Glader, B., Grace, R.F, López Lorenzo, J.L, Navarro Ordoñez, S., Nicoletti, E., Schwartz, J.D, Segovia, J.C, Sevilla, J., Shah, A.J, Zanella, A.
Published 2022